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Bridging East with West of Europe – a comparison of orphan drugs policies in Poland, Russia and the Netherlands

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Baran A., Czech M., Kooiker C., Hołownia M., Sykut- Cegielska J.

Acta Poloniae Pharmaceutica - Drug Research

2018

vol. 75

issue 6

1409-1422

The goal of this article is to provide an in-depth review of rare disease policies and the reimbursement of ODs in 3 European countries, two EU members (Poland, the Netherlands) and a non-EU one (Russia). A review of publicly available information on rare disorder policies and HTA processes was performed. Experts were consulted for unclear or scarce information. Russia has a five times higher frequency threshold for its rare disease definition than Poland and the Netherlands (both using the EU definition). The Netherlands has vastly increased its disease registries by instituting 300 expert centres via its National Plan, in Poland there are only 6 registries while in Russia one central registry exists. All 3 countries have an HTA process in place, however, the Russian one is relatively undeveloped. The access to ODs in the Netherlands is the broadest with 80 out of 83 EMA approved ODs reimbursed in 2015; Poland reimbursed 49, whereas Russia reimbursed 4 on the federal level and 43 in Moscow region. In all countries new rare disease policies are under development. The availability of healthcare systems solutions and the reimbursement of ODs differs greatly in all 3 countries, mainly in Russia. Even though both states are EU member with common regulations and access to EMA approved drugs, marked differences between Poland and the Netherlands in the range of policies, access to treatments and screening programs exist.

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1 Acta Poloniae Pharmaceutica - Drug Research

1 2018

1 Baran A.

1 Czech M.

1 Hołownia M.

1 Kooiker C.

1 Sykut- Cegielska J.

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Bridging East with West of Europe – a comparison of orphan drugs policies in Poland, Russia and the Netherlands